@misc {TN_libero_mab2,
author = { Mah, Jean K. AND Clemens, Paula R. AND Guglieri, Michela AND Smith, Edward C. AND Finkel, Richard S. AND Tulinius, Mar AND Nevo, Yoram AND Ryan, Monique M. AND Webster, Richard AND Castro, Diana AND Kuntz, Nancy L. AND McDonald, Craig M. AND Damsker, Jesse M. AND Schwartz, Benjamin D. AND Mengle-Gaw, Laurel J. AND Jackowski, Stefan AND Stimpson, Georgia AND Ridout, Deborah A. AND Ayyar-Gupta, Vandana AND Baranello, Giovanni AND Manzur, Adnan Y. AND Muntoni, Francesco AND Gordish-Dressman, Heather AND Leinonen, Mika AND Ward, Leanne M. AND Hoffman, Eric P. AND Dang, Utkarsh J. AND Muntoni, Francesco AND Manzur, Adnan AND Baranello, Giovanni AND Robb, Stephanie AND Quinlivan, Ros AND Sarkozy, Anna AND Munot, Pinki AND Main, Marion AND Abbot, Lianne AND Straub, Volker AND Guglieri, Michela AND Bertolli, Chiara AND Mayhew, Anna AND Muni-Lofra, Robert AND James, Meredith AND Sodhi, Jassi AND Parasuraman, Deepak AND Alhaswani, Zoya AND McMurchie, Heather AND Rabb, Rosanna AND Childs, Anne-Marie AND Pysden, Karen AND Pallant, Lindsey AND Small, Tiffany AND Spinty, Stefan AND Madhu, Rajesh AND Shillington, Alison AND Gregson, Sarah AND Wraige, Elizabeth AND Jungbluth, Heinz AND Gowda, Vasantha AND Sheehan, Jennie AND Hughes, Imelda AND Warner, Sinead AND Davies, Emily AND Willis, Tracey AND Kulshrestha, Richa AND Emery, Nicholas AND Strachan, Kate AND Ong, Min AND White, Kay AND Skone, Kate AND Gibbon, Frances AND Parsons, Bethan AND Majumdar, Anirban AND Vijaykumar, Kayal AND Mason, Faye AND Frimpong-Ansah, Claire AND Naismith, Karen AND Burslem, Julie AND Horrocks, Iain AND Di Marco, Marina AND Brown, Sarah AND Williamson, Sarah AND Spencer, Kirstie AND Chow, Gabby AND de Goede, Christian AND Selley, Andrea AND Thomas, Neil AND Illingworth, Marjorie AND Greary, Michelle AND Palmer, Jenni AND White, Cathy AND Greenfield, Kate AND Nic Fhirleinn, Grainne AND Douglas, Melanie AND Tiraputhi, Sandya AND Hussain, Nahin AND Julien, Yvonne AND Ambegaonkar, Gautam AND Krishnakumar, Deepa AND Taylor, Jacqui AND Tewnion, Jane AND Stephens, Elma AND Chandratre, Saleel AND Ramdas, Sithara AND Ramjattan, Hayley AND Baxter, Alex AND Eadie, Clare AND McDonald, Craig M AND Henricson, Erik K AND Abresch, R Ted AND Joyce, Nanette C AND Viswanathan, Venkatarman AND Chidambaranathan, Sivaprakasam AND Biggar, Douglas AND McAdam, Laura C AND Mah, Jean K AND Tulinius, Mar AND Cnaan, Avital AND Morgenroth, Lauren P AND Leshner, Robert AND Tesi-Rocha, Carolina AND Thangarajh, Mathula AND Duong, Tina AND Kornberg, Andrew AND Ryan, Monique AND Nevo, Yoram AND Dubrovsky, Alberto AND Clemens, Paula R AND Abdel-Hamid, Hoda AND Connolly, Anne M AND Pestronk, Alan AND Teasley, Jean AND Bertorini, Tulio E AND Webster, Richard AND Kolski, Hanna AND Kuntz, Nancy AND Driscoll, Sherilyn W AND Bodensteiner, John B AND Carlo, Jose AND Gorni, Ksenija AND Lotze, Timothy AND Day, John W AND Karachunski, Peter },
title = { Efficacy and Safety of Vamorolone in Duchenne Muscular Dystrophy : A 30-Month Nonrandomized Controlled Open-Label Extension Trial A 30-Month Nonrandomized Controlled Open-Label Extension Trial },
publisher = {American Medical Association (AMA)},
isbn = {2574-3805},
year = {2022},
url = { http://slubdd.de/katalog?TN_libero_mab2 }
}
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