%0 Generic
%T Splice-correcting oligonucleotides restore BTK function in X-linked agammaglobulinemia model
%A Bestas, Burcu
%A Moreno, Pedro M.D.
%A Blomberg, K. Emelie M.
%A Mohammad, Dara K.
%A Saleh, Amer F.
%A Sutlu, Tolga
%A Nordin, Joel Z.
%A Guterstam, Peter
%A Gustafsson, Manuela O.
%A Kharazi, Shabnam
%A Piątosa, Barbara
%A Roberts, Thomas C.
%A Behlke, Mark A.
%A Wood, Matthew J.A.
%A Gait, Michael J.
%A Lundin, Karin E.
%A El Andaloussi, Samir
%A Månsson, Robert
%A Berglöf, Anna
%A Wengel, Jesper
%A Smith, C.I. Edvard
%I American Society for Clinical Investigation
%@ 0021-9738
%D 2014
%C American Society for Clinical Investigation
%U http://slubdd.de/katalog?TN_libero_mab2
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