Skip to contents Zink, Sheila [Author] Präklinische ex vivo-Effekte von CFTR-Modulatoren an humanen Rektumbiopsien zur Medikamentenentwicklung bei Mukoviszidose Books View online Schließen > Access https://d-nb.info/1234983397/34 kostenfrei Show more show less Close > Bookmarks You can manage bookmarks using lists, please log in to your user account for this. Berlin: Medizinische Fakultät Charité - Universitätsmedizin Berlin, 2021 Bushby, Kate [Author]; Mcdonald, Craig M. [Author] Ataluren treatment of patients with nonsense mutation dystrophinopathy: ataluren for dystrophinopathy Books View online Schließen > Access More information on the full text Full access (via DOI) Show more show less Close > Bookmarks You can manage bookmarks using lists, please log in to your user account for this. New York, NY: Wiley, 2014 Published in: Muscle & nerve ; 50, 4 (2014), 477-487 Campbell, Craig [Author]; Kirschner, Janbernd [Author]; Muntoni, Francesco [Author] Meta-analyses of ataluren randomized controlled trials in nonsense mutation Duchenne muscular dystrophy Books View online Schließen > Access Full access (via DOI) More information on the full text Show more show less Close > Bookmarks You can manage bookmarks using lists, please log in to your user account for this. London: Future Medicine, 2020 Published in: Journal of comparative effectiveness research ; 9, 14 (2020), 973-984 Ryan, Nicola J. Ataluren: First Global Approval Articles View online Schließen > Access Close > Bookmarks You can manage bookmarks using lists, please log in to your user account for this. Springer Science and Business Media LLC, 2014 Published in: Drugs Lentini, Laura; Melfi, Raffaella; Cancemi, Patrizia; Pibiri, Ivana; Di Leonardo, Aldo Caffeine boosts Ataluren's readthrough activity Articles View online Schließen > Access Close > Bookmarks You can manage bookmarks using lists, please log in to your user account for this. Elsevier BV, 2019 Published in: Heliyon Duchenne-Muskeldystrophie: Ataluren bei Nonsensemutation Articles View online Schließen > Access Close > Bookmarks You can manage bookmarks using lists, please log in to your user account for this. Georg Thieme Verlag KG, 2018 Published in: Fortschritte der Neurologie · Psychiatrie Berger, Joachim; Li, Mei; Berger, Silke; Meilak, Michelle; Rientjes, Jeanette; Currie, Peter D. Effect of Ataluren on dystrophin mutations Articles View online Schließen > Access Close > Bookmarks You can manage bookmarks using lists, please log in to your user account for this. Wiley, 2020 Published in: Journal of Cellular and Molecular Medicine Morkous, Sameh S. Treatment with Ataluren for Duchene Muscular Dystrophy Articles View online Schließen > Access Close > Bookmarks You can manage bookmarks using lists, please log in to your user account for this. Pediatric Neurology Briefs Publishers, 2020 Published in: Pediatric Neurology Briefs Werner, Christian; Tian, Cuixia; Kong, Robert; O’Mara, Edward; Schilling, Traci; Trifillis, Panayiota; McIntosh, Joseph; Renfroe, J. Ben Ataluren in Patients Aged 2 to Conference Proceedings View online Schließen > Access Full access (via DOI) Show more show less Close > Bookmarks You can manage bookmarks using lists, please log in to your user account for this. Georg Thieme Verlag KG, 2019 Published in: Neuropediatrics Siddiqui, Nadeem; Sonenberg, Nahum Proposing a mechanism of action for ataluren Articles View online Schließen > Access Close > Bookmarks You can manage bookmarks using lists, please log in to your user account for this. Proceedings of the National Academy of Sciences, 2016 Published in: Proceedings of the National Academy of Sciences Siddiqui, Nadeem; Sonenberg, Nahum Proposing a mechanism of action for ataluren Articles View online Schließen > Access Close > Bookmarks You can manage bookmarks using lists, please log in to your user account for this. National Academy of Sciences, 2016 Published in: Proceedings of the National Academy of Sciences of the United States of America Peltz, Stuart W.; Welch, Ellen M.; Jacobson, Allan; Trotta, Christopher R.; Naryshkin, Nikolai; Sweeney, H. Lee; Bedwell, David M. Nonsense suppression activity of PTC124 (ataluren) Articles View online Schließen > Access Close > Bookmarks You can manage bookmarks using lists, please log in to your user account for this. Proceedings of the National Academy of Sciences, 2009 Published in: Proceedings of the National Academy of Sciences Facharztmagazine, Redaktion Länger motorisch aktiv bei Duchenne-Muskeldystrophie mit Ataluren Articles View online Schließen > Access Close > Bookmarks You can manage bookmarks using lists, please log in to your user account for this. Springer Science and Business Media LLC, 2023 Published in: Pädiatrie Michorowska, Sylwia Ataluren—Promising Therapeutic Premature Termination Codon Readthrough Frontrunner Articles View online Schließen > Access Close > Bookmarks You can manage bookmarks using lists, please log in to your user account for this. MDPI AG, 2021 Published in: Pharmaceuticals Michael, Eva; Sofou, Kalliopi; Wahlgren, Lisa; Kroksmark, Anna-Karin; Tulinius, Már Long term treatment with ataluren—the Swedish experience Articles View online Schließen > Access Close > Bookmarks You can manage bookmarks using lists, please log in to your user account for this. Springer Science and Business Media LLC, 2021 Published in: BMC Musculoskeletal Disorders Kong, Ronald; Laskin, Oscar L.; Kaushik, Diksha; Jin, Fengbin; Ma, Jiyuan; McIntosh, Joseph; Souza, Marcio; Almstead, Neil Ataluren Pharmacokinetics in Healthy Japanese and Caucasian Subjects Articles View online Schließen > Access Close > Bookmarks You can manage bookmarks using lists, please log in to your user account for this. Wiley, 2019 Published in: Clinical Pharmacology in Drug Development NICE issues final guidance recommending ataluren for DMD Articles View online Schließen > Access Close > Bookmarks You can manage bookmarks using lists, please log in to your user account for this. Springer Science and Business Media LLC, 2016 Published in: PharmacoEconomics & Outcomes News NICE recommends ataluren for selected patients with MD Articles View online Schließen > Access Close > Bookmarks You can manage bookmarks using lists, please log in to your user account for this. Springer Science and Business Media LLC, 2016 Published in: PharmacoEconomics & Outcomes News Kandidat für den Galenus-Preis 2015: Ataluren gegen Duchenne-Muskeldystrophie Articles View online Schließen > Access Close > Bookmarks You can manage bookmarks using lists, please log in to your user account for this. Springer Science and Business Media LLC, 2015 Published in: Orthopädie & Rheuma NICE asks for more evidence to justify cost of ataluren Articles View online Schließen > Access Close > Bookmarks You can manage bookmarks using lists, please log in to your user account for this. Springer Science and Business Media LLC, 2015 Published in: PharmacoEconomics & Outcomes News
Zink, Sheila [Author] Präklinische ex vivo-Effekte von CFTR-Modulatoren an humanen Rektumbiopsien zur Medikamentenentwicklung bei Mukoviszidose Books View online Schließen > Access https://d-nb.info/1234983397/34 kostenfrei Show more show less Close > Bookmarks You can manage bookmarks using lists, please log in to your user account for this. Berlin: Medizinische Fakultät Charité - Universitätsmedizin Berlin, 2021
Bushby, Kate [Author]; Mcdonald, Craig M. [Author] Ataluren treatment of patients with nonsense mutation dystrophinopathy: ataluren for dystrophinopathy Books View online Schließen > Access More information on the full text Full access (via DOI) Show more show less Close > Bookmarks You can manage bookmarks using lists, please log in to your user account for this. New York, NY: Wiley, 2014 Published in: Muscle & nerve ; 50, 4 (2014), 477-487
Campbell, Craig [Author]; Kirschner, Janbernd [Author]; Muntoni, Francesco [Author] Meta-analyses of ataluren randomized controlled trials in nonsense mutation Duchenne muscular dystrophy Books View online Schließen > Access Full access (via DOI) More information on the full text Show more show less Close > Bookmarks You can manage bookmarks using lists, please log in to your user account for this. London: Future Medicine, 2020 Published in: Journal of comparative effectiveness research ; 9, 14 (2020), 973-984
Ryan, Nicola J. Ataluren: First Global Approval Articles View online Schließen > Access Close > Bookmarks You can manage bookmarks using lists, please log in to your user account for this. Springer Science and Business Media LLC, 2014 Published in: Drugs
Lentini, Laura; Melfi, Raffaella; Cancemi, Patrizia; Pibiri, Ivana; Di Leonardo, Aldo Caffeine boosts Ataluren's readthrough activity Articles View online Schließen > Access Close > Bookmarks You can manage bookmarks using lists, please log in to your user account for this. Elsevier BV, 2019 Published in: Heliyon
Duchenne-Muskeldystrophie: Ataluren bei Nonsensemutation Articles View online Schließen > Access Close > Bookmarks You can manage bookmarks using lists, please log in to your user account for this. Georg Thieme Verlag KG, 2018 Published in: Fortschritte der Neurologie · Psychiatrie
Berger, Joachim; Li, Mei; Berger, Silke; Meilak, Michelle; Rientjes, Jeanette; Currie, Peter D. Effect of Ataluren on dystrophin mutations Articles View online Schließen > Access Close > Bookmarks You can manage bookmarks using lists, please log in to your user account for this. Wiley, 2020 Published in: Journal of Cellular and Molecular Medicine
Morkous, Sameh S. Treatment with Ataluren for Duchene Muscular Dystrophy Articles View online Schließen > Access Close > Bookmarks You can manage bookmarks using lists, please log in to your user account for this. Pediatric Neurology Briefs Publishers, 2020 Published in: Pediatric Neurology Briefs
Werner, Christian; Tian, Cuixia; Kong, Robert; O’Mara, Edward; Schilling, Traci; Trifillis, Panayiota; McIntosh, Joseph; Renfroe, J. Ben Ataluren in Patients Aged 2 to Conference Proceedings View online Schließen > Access Full access (via DOI) Show more show less Close > Bookmarks You can manage bookmarks using lists, please log in to your user account for this. Georg Thieme Verlag KG, 2019 Published in: Neuropediatrics
Siddiqui, Nadeem; Sonenberg, Nahum Proposing a mechanism of action for ataluren Articles View online Schließen > Access Close > Bookmarks You can manage bookmarks using lists, please log in to your user account for this. Proceedings of the National Academy of Sciences, 2016 Published in: Proceedings of the National Academy of Sciences
Siddiqui, Nadeem; Sonenberg, Nahum Proposing a mechanism of action for ataluren Articles View online Schließen > Access Close > Bookmarks You can manage bookmarks using lists, please log in to your user account for this. National Academy of Sciences, 2016 Published in: Proceedings of the National Academy of Sciences of the United States of America
Peltz, Stuart W.; Welch, Ellen M.; Jacobson, Allan; Trotta, Christopher R.; Naryshkin, Nikolai; Sweeney, H. Lee; Bedwell, David M. Nonsense suppression activity of PTC124 (ataluren) Articles View online Schließen > Access Close > Bookmarks You can manage bookmarks using lists, please log in to your user account for this. Proceedings of the National Academy of Sciences, 2009 Published in: Proceedings of the National Academy of Sciences
Facharztmagazine, Redaktion Länger motorisch aktiv bei Duchenne-Muskeldystrophie mit Ataluren Articles View online Schließen > Access Close > Bookmarks You can manage bookmarks using lists, please log in to your user account for this. Springer Science and Business Media LLC, 2023 Published in: Pädiatrie
Michorowska, Sylwia Ataluren—Promising Therapeutic Premature Termination Codon Readthrough Frontrunner Articles View online Schließen > Access Close > Bookmarks You can manage bookmarks using lists, please log in to your user account for this. MDPI AG, 2021 Published in: Pharmaceuticals
Michael, Eva; Sofou, Kalliopi; Wahlgren, Lisa; Kroksmark, Anna-Karin; Tulinius, Már Long term treatment with ataluren—the Swedish experience Articles View online Schließen > Access Close > Bookmarks You can manage bookmarks using lists, please log in to your user account for this. Springer Science and Business Media LLC, 2021 Published in: BMC Musculoskeletal Disorders
Kong, Ronald; Laskin, Oscar L.; Kaushik, Diksha; Jin, Fengbin; Ma, Jiyuan; McIntosh, Joseph; Souza, Marcio; Almstead, Neil Ataluren Pharmacokinetics in Healthy Japanese and Caucasian Subjects Articles View online Schließen > Access Close > Bookmarks You can manage bookmarks using lists, please log in to your user account for this. Wiley, 2019 Published in: Clinical Pharmacology in Drug Development
NICE issues final guidance recommending ataluren for DMD Articles View online Schließen > Access Close > Bookmarks You can manage bookmarks using lists, please log in to your user account for this. Springer Science and Business Media LLC, 2016 Published in: PharmacoEconomics & Outcomes News
NICE recommends ataluren for selected patients with MD Articles View online Schließen > Access Close > Bookmarks You can manage bookmarks using lists, please log in to your user account for this. Springer Science and Business Media LLC, 2016 Published in: PharmacoEconomics & Outcomes News
Kandidat für den Galenus-Preis 2015: Ataluren gegen Duchenne-Muskeldystrophie Articles View online Schließen > Access Close > Bookmarks You can manage bookmarks using lists, please log in to your user account for this. Springer Science and Business Media LLC, 2015 Published in: Orthopädie & Rheuma
NICE asks for more evidence to justify cost of ataluren Articles View online Schließen > Access Close > Bookmarks You can manage bookmarks using lists, please log in to your user account for this. Springer Science and Business Media LLC, 2015 Published in: PharmacoEconomics & Outcomes News
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