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  1. Ziegler, Andreas [Author]; Wilichowski, Ekkehard [Author]; Schara, Ulrike [Author]; Hahn, Andreas [Author]; Müller-Felber, Wolfgang [Author]; Johannsen, Jessika [Author]; Hagen, Maja von der [Author]; Moers, Arpad von [Author]; Stoltenburg, Corinna [Author]; Saffari, Afshin [Author]; Walter, Maggie C. [Author]; Husain, Ralf A. [Author]; Pechmann, Astrid [Author]; Köhler, Cornelia [Author]; Horber, Veronka [Author]; Schwartz, Oliver [Author]; Kirschner, Janbernd [Author]

    Handlungsempfehlungen zur Gentherapie der spinalen Muskelatrophie mit Onasemnogene Abeparvovec – AVXS-101 : Konsensuspapier der deutschen Vertretung der Gesellschaft für Neuropädiatrie (GNP) und der deutschen Behandlungszentren unter Mitwirkung des Medizinisch-Wissenschaftlichen Beirates der Deutschen Gesellschaft für Muskelkranke (DGM) e. V.

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    Berlin; Heidelberg: Springer Nature, 2020

    Published in: Der Nervenarzt ; 91, 6 (2020), 518-529

  2. Ziegler, Andreas [Author]; Wilichowski, Ekkehard [Author]; Schara, Ulrike [Author]; Hahn, Andreas [Author]; Müller-Felber, Wolfgang [Author]; Johannsen, Jessika [Author]; Hagen, Maja von der [Author]; Moers, Arpad von [Author]; Stoltenburg, Corinna [Author]; Saffari, Afshin [Author]; Walter, Maggie C. [Author]; Husain, Ralf [Author]; Pechmann, Astrid [Author]; Köhler, Cornelia [Author]; Horber, Veronka [Author]; Schwartz, Oliver [Author]; Kirschner, Janbernd [Author]

    Handlungsempfehlungen zur Gentherapie der spinalen Muskelatrophie mit Onasemnogene Abeparvovec - AVXS-101 : Konsensuspapier der deutschen Vertretung der Gesellschaft für Neuropädiatrie (GNP) und der deutschen Behandlungszentren unter Mitwirkung des Medizinisch-Wissenschaftlichen Beirates der Deutschen Gesellschaft für Muskelkranke (DGM) e.V.

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    11 May 2020

    Published in: Der Nervenarzt ; 91(2020), 6, Seite 518-529

  3. Müller-Felber, Wolfgang [Author]; Blaschek, Astrid [Author]; Schwartz, Oliver [Author]; Gläser, Dieter [Author]; Nennstiel, Uta [Author]; Brockow, Inken [Author]; Wirth, Brunhilde [Author]; Burggraf, Siegfried [Author]; Röschinger, Wulf [Author]; Becker, Marc [Author]; Durner, Jürgen [Author]; Eggermann, Katja [Author]; Kölbel, Heike [Author]; Müller, Christine [Author]; Hannibal, Iris [Author]; Olgemöller, Bernd [Author]; Schara, Ulrike [Author]; von Moers, Arpad [Author]; Trollmann, Regina [Author]; Johannssen, Jessika [Author]; Ziegler, Andreas [Author]; Cirak, Sebahattin [Author]; Hahn, Andreas [Author]; von der Hagen, Maja [Author]; [...]

    Newbornscreening SMA : from pilot project to nationwide screening in Germany

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    3 January 2023

    Published in: Journal of neuromuscular diseases ; 10(2023), 1, Seite 55-65

  4. Pechmann, Astrid [Author]; Behrens, Max [Author]; Dörnbrack, Katharina [Author]; Tassoni, Adrian [Author]; Wenzel, Franziska [Author]; Stein, Sabine [Author]; Vogt, Sibylle [Author]; Zöller, Daniela [Author]; Bernert, Günther [Author]; Hagenacker, Tim [Author]; Schara-Schmidt, Ulrike [Author]; Walter, Maggie C. [Author]; Steinbach, Meike [Author]; Blaschek, Astrid [Author]; Baumann, Matthias [Author]; Baumgartner, Manuela [Author]; Becker, Benedikt [Author]; Flotats-Bastardas, Marina [Author]; Friese, Johannes [Author]; Günther, Rene [Author]; Hahn, Andreas [Author]; Küpper, Hanna [Author]; Johannsen, Jessika [Author]; Kamm, Christoph [Author]; [...]

    Improvements in walking distance during nusinersen treatment : a prospective 3-year SMArtCARE registry study

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    3 January 2023

    Published in: Journal of neuromuscular diseases ; 10(2023), 1, Seite 29-40

  5. Pfeiffer, Ernst; von Moers, Arpad

    CAMPTOCORMIA IN AN ADOLESCENT

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    Elsevier BV, 2000

    Published in: Journal of the American Academy of Child & Adolescent Psychiatry

  6. Berthold, Oliver; Frericks, Bernd; John, Thilo; Clemens, Vera; Fegert, Jörg M.; von Moers, Arpad

    Abuse as a Cause of Childhood Fractures

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    Deutscher Arzte-Verlag GmbH, 2018

    Published in: Deutsches Ärzteblatt international

  7. Endesfelder, Stefanie; Kliche, Alexander; Lochmüller, Hanns; von Moers, Arpad; Speer, Astrid

    Antisense oligonucleotides and short interfering RNAs silencing the cyclin-dependent kinase inhibitor p21 improve proliferation of Duchenne muscular dystrophy patients’ primary skeletal myoblasts

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    Springer Science and Business Media LLC, 2005

    Published in: Journal of Molecular Medicine

  8. Horn, Denise; Tönnies, Holger; Neitzel, Heidemarie; Wahl, Dagmar; Hinkel, Georg Klaus; Moers, Arpad von; Bartsch, Oliver

    Minimal clinical expression of the holoprosencephaly spectrum and of Currarino syndrome due to different cytogenetic rearrangements deleting the sonic hedgehog gene and the HLXB9 gene at 7q36.3

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    Wiley, 2004

    Published in: American Journal of Medical Genetics Part A