• Media type: E-Book; Special Print
  • Title: Experiences of caregivers of children with spinal muscular atrophy participating in the expanded access program for nusinersen: a longitudinal qualitative study
  • Contributor: Kiefer, Petra [VerfasserIn]; Kirschner, Janbernd [VerfasserIn]; Pechmann, Astrid [VerfasserIn]; Langer, Thorsten [VerfasserIn]
  • imprint: London: BioMed Central, 2020
  • Published in: Orphanet journal of rare diseases ; 15, 1 (2020), 194
  • Extent: 1 Online-Ressource (9 Seiten)
  • Language: English
  • DOI: 10.1186/s13023-020-01477-7
  • ISSN: 1750-1172
  • Identifier:
  • Keywords: Spinale Muskelatrophie ; Kinderkrankenpflege
  • Origination:
  • Footnote:
  • Access State: Open Access