• Media type: E-Article
  • Title: A phase I/II study on intracerebroventricular tralesinidase alfa in patients with Sanfilippo syndrome type B
  • Contributor: Nicole Muschol; Anja Koehn; Katharina von Cossel; Ilyas Okur; Fatih Ezgu; Paul Harmatz; Maria J. de Castro Lopez; Maria Luz Couce; Shuan-Pei Lin; Spyros Batzios; Maureen Cleary; Martha Solano; Igor Nestrasil; Brian Kaufman; Adam J. Shaywitz; Stephen M. Maricich; Bernice Kuca; Joseph Kovalchin; Eric Zanelli
  • imprint: 2023
  • Published in: The Journal of Clinical Investigation
  • Language: English
  • ISSN: 1558-8238
  • Origination:
  • Footnote:
  • Access State: Open Access