Nicole Muschol;
Anja Koehn;
Katharina von Cossel;
Ilyas Okur;
Fatih Ezgu;
Paul Harmatz;
Maria J. de Castro Lopez;
Maria Luz Couce;
Shuan-Pei Lin;
Spyros Batzios;
Maureen Cleary;
Martha Solano;
Igor Nestrasil;
Brian Kaufman;
Adam J. Shaywitz;
Stephen M. Maricich;
Bernice Kuca;
Joseph Kovalchin;
Eric Zanelli
A phase I/II study on intracerebroventricular tralesinidase alfa in patients with Sanfilippo syndrome type B
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Media type:
E-Article
Title:
A phase I/II study on intracerebroventricular tralesinidase alfa in patients with Sanfilippo syndrome type B
Contributor:
Nicole Muschol;
Anja Koehn;
Katharina von Cossel;
Ilyas Okur;
Fatih Ezgu;
Paul Harmatz;
Maria J. de Castro Lopez;
Maria Luz Couce;
Shuan-Pei Lin;
Spyros Batzios;
Maureen Cleary;
Martha Solano;
Igor Nestrasil;
Brian Kaufman;
Adam J. Shaywitz;
Stephen M. Maricich;
Bernice Kuca;
Joseph Kovalchin;
Eric Zanelli
imprint:
2023
Published in:The Journal of Clinical Investigation