Media type: E-Article Title: Study of Intraventricular Cerliponase Alfa for CLN2 Disease Contributor: Schulz, Angela; Ajayi, Temitayo; Specchio, Nicola; de Los Reyes, Emily; Gissen, Paul; Ballon, Douglas; Dyke, Jonathan P.; Cahan, Heather; Slasor, Peter; Jacoby, David; Kohlschütter, Alfried imprint: Massachusetts Medical Society, 2018 Published in: New England Journal of Medicine Language: English DOI: 10.1056/nejmoa1712649 ISSN: 0028-4793; 1533-4406 Origination: Footnote: Access State: Open Access