• Media type: E-Article
  • Title: Study of Intraventricular Cerliponase Alfa for CLN2 Disease
  • Contributor: Schulz, Angela; Ajayi, Temitayo; Specchio, Nicola; de Los Reyes, Emily; Gissen, Paul; Ballon, Douglas; Dyke, Jonathan P.; Cahan, Heather; Slasor, Peter; Jacoby, David; Kohlschütter, Alfried
  • imprint: Massachusetts Medical Society, 2018
  • Published in: New England Journal of Medicine
  • Language: English
  • DOI: 10.1056/nejmoa1712649
  • ISSN: 0028-4793; 1533-4406
  • Origination:
  • Footnote:
  • Access State: Open Access