• Media type: E-Article
  • Title: iPSC-Derived Intestinal Organoids from Cystic Fibrosis Patients Acquire CFTR Activity upon TALEN-Mediated Repair of the p.F508del Mutation
  • Contributor: Fleischer, Aarne; Vallejo-Díez, Sara; Martín-Fernández, José María; Sánchez-Gilabert, Almudena; Castresana, Mónica; del Pozo, Angel; Esquisabel, Amaia; Ávila, Silvia; Castrillo, José Luis; Gaínza, Eusebio; Pedraz, José Luis; Viñas, Miguel; Bachiller, Daniel
  • imprint: Elsevier BV, 2020
  • Published in: Molecular Therapy - Methods & Clinical Development
  • Language: English
  • DOI: 10.1016/j.omtm.2020.04.005
  • ISSN: 2329-0501
  • Origination:
  • Footnote:
  • Access State: Open Access