• Media type: E-Article
  • Title: Full-length ATP7B reconstituted through protein trans-splicing corrects Wilson disease in mice
  • Contributor: Padula, Agnese; Petruzzelli, Raffaella; Philbert, Sasha A.; Church, Stephanie J.; Esposito, Federica; Campione, Severo; Monti, Marcello; Capolongo, Filomena; Perna, Claudia; Nusco, Edoardo; Schmidt, Hartmut H.; Auricchio, Alberto; Cooper, Garth J.S.; Polishchuk, Roman; Piccolo, Pasquale
  • Published: Elsevier BV, 2022
  • Published in: Molecular Therapy - Methods & Clinical Development, 26 (2022), Seite 495-504
  • Language: English
  • DOI: 10.1016/j.omtm.2022.08.004
  • ISSN: 2329-0501
  • Origination:
  • Footnote:
  • Access State: Open Access