• Media type: E-Article
  • Title: Sustained long-term disease correction in a murine model of MPSII following stem cell gene therapy
  • Contributor: Ellison, Stuart; Liao, Aiyin; Gleitz, Hélène F.E.; Parker, Helen; Booth, Laura; Robinson, John; Wood, Shaun; Taylor, Jessica; Holley, Rebecca; Bigger, Brian W.
  • imprint: Elsevier BV, 2023
  • Published in: Molecular Therapy - Methods & Clinical Development
  • Language: English
  • DOI: 10.1016/j.omtm.2023.101127
  • ISSN: 2329-0501
  • Keywords: Genetics ; Molecular Biology ; Molecular Medicine
  • Origination:
  • Footnote:
  • Access State: Open Access