• Media type: E-Article
  • Title: Targeted Repair of p47-CGD in iPSCs by CRISPR/Cas9: Functional Correction without Cleavage in the Highly Homologous Pseudogenes
  • Contributor: Klatt, Denise; Cheng, Erica; Philipp, Friederike; Selich, Anton; Dahlke, Julia; Schmidt, Reinhold E.; Schott, Juliane W.; Büning, Hildegard; Hoffmann, Dirk; Thrasher, Adrian J.; Schambach, Axel
  • imprint: Elsevier BV, 2019
  • Published in: Stem Cell Reports
  • Language: English
  • DOI: 10.1016/j.stemcr.2019.08.008
  • ISSN: 2213-6711
  • Keywords: Cell Biology ; Developmental Biology ; Genetics ; Biochemistry
  • Origination:
  • Footnote:
  • Access State: Open Access