Media type: E-Article Title: Is hematopoietic stem cell transplantation a therapeutic option for mucolipidosis type II? Contributor: Ammer, Luise Sophie; Pohl, Sandra; Breyer, Sandra Rafaela; Aries, Charlotte; Denecke, Jonas; Perez, Anna; Petzoldt, Martin; Schrum, Johanna; Müller, Ingo; Muschol, Nicole Maria imprint: Elsevier BV, 2021 Published in: Molecular Genetics and Metabolism Reports Language: English DOI: 10.1016/j.ymgmr.2020.100704 ISSN: 2214-4269 Keywords: Endocrinology ; Genetics ; Molecular Biology Origination: Footnote: Access State: Open Access