• Media type: E-Article
  • Title: Long-term efficacy and safety of eladocagene exuparvovec in patients with AADC deficiency
  • Contributor: Tai, Chun-Hwei; Lee, Ni-Chung; Chien, Yin-Hsiu; Byrne, Barry J.; Muramatsu, Shin-Ichi; Tseng, Sheng-Hong; Hwu, Wuh-Liang
  • imprint: Elsevier BV, 2022
  • Published in: Molecular Therapy
  • Language: English
  • DOI: 10.1016/j.ymthe.2021.11.005
  • ISSN: 1525-0016
  • Origination:
  • Footnote:
  • Access State: Open Access