Media type: E-Article Title: Long-term efficacy and safety of eladocagene exuparvovec in patients with AADC deficiency Contributor: Tai, Chun-Hwei; Lee, Ni-Chung; Chien, Yin-Hsiu; Byrne, Barry J.; Muramatsu, Shin-Ichi; Tseng, Sheng-Hong; Hwu, Wuh-Liang imprint: Elsevier BV, 2022 Published in: Molecular Therapy Language: English DOI: 10.1016/j.ymthe.2021.11.005 ISSN: 1525-0016 Origination: Footnote: Access State: Open Access