Media type: E-Article Title: 201. Neuron-Specific Systemic Gene Therapy for Aromatic L-Amino Acid Decarboxylase (AADC) Deficiency Contributor: Lee, Ni-Chung; Muramatsu, Shin-Ichi; Chien, Yin-Hsiu; Chen, Pin-Wen; Tzen, Kai-Yuan; Byrne, Barry J.; Hwu, Wuh-Liang imprint: Elsevier BV, 2015 Published in: Molecular Therapy Language: English DOI: 10.1016/s1525-0016(16)33806-0 ISSN: 1525-0016 Keywords: Drug Discovery ; Pharmacology ; Genetics ; Molecular Biology ; Molecular Medicine Origination: Footnote: Access State: Open Access