• Media type: E-Article
  • Title: 201. Neuron-Specific Systemic Gene Therapy for Aromatic L-Amino Acid Decarboxylase (AADC) Deficiency
  • Contributor: Lee, Ni-Chung; Muramatsu, Shin-Ichi; Chien, Yin-Hsiu; Chen, Pin-Wen; Tzen, Kai-Yuan; Byrne, Barry J.; Hwu, Wuh-Liang
  • imprint: Elsevier BV, 2015
  • Published in: Molecular Therapy
  • Language: English
  • DOI: 10.1016/s1525-0016(16)33806-0
  • ISSN: 1525-0016
  • Keywords: Drug Discovery ; Pharmacology ; Genetics ; Molecular Biology ; Molecular Medicine
  • Origination:
  • Footnote:
  • Access State: Open Access