• Media type: E-Article
  • Title: Discovery of Small Molecule Splicing Modulators of Survival Motor Neuron-2 (SMN2) for the Treatment of Spinal Muscular Atrophy (SMA)
  • Contributor: Cheung, Atwood K.; Hurley, Brian; Kerrigan, Ryan; Shu, Lei; Chin, Donovan N.; Shen, Yiping; O’Brien, Gary; Sung, Moo Je; Hou, Ying; Axford, Jake; Cody, Emma; Sun, Robert; Fazal, Aleem; Fridrich, Cary; Sanchez, Carina C.; Tomlinson, Ronald C.; Jain, Monish; Deng, Lin; Hoffmaster, Keith; Song, Cheng; Van Hoosear, Mailin; Shin, Youngah; Servais, Rebecca; Towler, Christopher; [...]
  • Published: American Chemical Society (ACS), 2018
  • Published in: Journal of Medicinal Chemistry, 61 (2018) 24, Seite 11021-11036
  • Language: English
  • DOI: 10.1021/acs.jmedchem.8b01291
  • ISSN: 1520-4804; 0022-2623
  • Origination:
  • Footnote: