Media type: E-Article Title: Gene Therapy in Patient-specific Stem Cell Lines and a Preclinical Model of Retinitis Pigmentosa With Membrane Frizzled-related Protein Defects Contributor: Li, Yao; Wu, Wen-Hsuan; Hsu, Chun-Wei; Nguyen, Huy V; Tsai, Yi-Ting; Chan, Lawrence; Nagasaki, Takayuki; Maumenee, Irene H; Yannuzzi, Lawrence A; Hoang, Quan V; Hua, Haiqing; Egli, Dieter; Tsang, Stephen H imprint: Elsevier BV, 2014 Published in: Molecular Therapy Language: English DOI: 10.1038/mt.2014.100 ISSN: 1525-0016 Origination: Footnote: Access State: Open Access