• Media type: E-Article
  • Title: Gene Therapy in Patient-specific Stem Cell Lines and a Preclinical Model of Retinitis Pigmentosa With Membrane Frizzled-related Protein Defects
  • Contributor: Li, Yao; Wu, Wen-Hsuan; Hsu, Chun-Wei; Nguyen, Huy V; Tsai, Yi-Ting; Chan, Lawrence; Nagasaki, Takayuki; Maumenee, Irene H; Yannuzzi, Lawrence A; Hoang, Quan V; Hua, Haiqing; Egli, Dieter; Tsang, Stephen H
  • imprint: Elsevier BV, 2014
  • Published in: Molecular Therapy
  • Language: English
  • DOI: 10.1038/mt.2014.100
  • ISSN: 1525-0016
  • Origination:
  • Footnote:
  • Access State: Open Access