Meyer, Kathrin;
Ferraiuolo, Laura;
Schmelzer, Leah;
Braun, Lyndsey;
McGovern, Vicki;
Likhite, Shibi;
Michels, Olivia;
Govoni, Alessandra;
Fitzgerald, Julie;
Morales, Pablo;
Foust, Kevin D;
Mendell, Jerry R;
Burghes, Arthur H M;
Kaspar, Brian K
Improving Single Injection CSF Delivery of AAV9-mediated Gene Therapy for SMA: A Dose–response Study in Mice and Nonhuman Primates
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Media type:
E-Article
Title:
Improving Single Injection CSF Delivery of AAV9-mediated Gene Therapy for SMA: A Dose–response Study in Mice and Nonhuman Primates
Contributor:
Meyer, Kathrin;
Ferraiuolo, Laura;
Schmelzer, Leah;
Braun, Lyndsey;
McGovern, Vicki;
Likhite, Shibi;
Michels, Olivia;
Govoni, Alessandra;
Fitzgerald, Julie;
Morales, Pablo;
Foust, Kevin D;
Mendell, Jerry R;
Burghes, Arthur H M;
Kaspar, Brian K
Published:
Elsevier BV, 2015
Published in:
Molecular Therapy, 23 (2015) 3, Seite 477-487