• Media type: E-Article
  • Title: Fetal gene therapy for neurodegenerative disease of infants
  • Contributor: Massaro, Giulia; Mattar, Citra N. Z.; Wong, Andrew M. S.; Sirka, Ernestas; Buckley, Suzanne M. K.; Herbert, Bronwen R.; Karlsson, Stefan; Perocheau, Dany P.; Burke, Derek; Heales, Simon; Richard-Londt, Angela; Brandner, Sebastian; Huebecker, Mylene; Priestman, David A.; Platt, Frances M.; Mills, Kevin; Biswas, Arijit; Cooper, Jonathan D.; Chan, Jerry K. Y.; Cheng, Seng H.; Waddington, Simon N.; Rahim, Ahad A.
  • imprint: Springer Science and Business Media LLC, 2018
  • Published in: Nature Medicine
  • Language: English
  • DOI: 10.1038/s41591-018-0106-7
  • ISSN: 1078-8956; 1546-170X
  • Origination:
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