• Media type: E-Article
  • Title: A high-fidelity Cas9 mutant delivered as a ribonucleoprotein complex enables efficient gene editing in human hematopoietic stem and progenitor cells
  • Contributor: Vakulskas, Christopher A.; Dever, Daniel P.; Rettig, Garrett R.; Turk, Rolf; Jacobi, Ashley M.; Collingwood, Michael A.; Bode, Nicole M.; McNeill, Matthew S.; Yan, Shuqi; Camarena, Joab; Lee, Ciaran M.; Park, So Hyun; Wiebking, Volker; Bak, Rasmus O.; Gomez-Ospina, Natalia; Pavel-Dinu, Mara; Sun, Wenchao; Bao, Gang; Porteus, Matthew H.; Behlke, Mark A.
  • Published: Springer Science and Business Media LLC, 2018
  • Published in: Nature Medicine, 24 (2018) 8, Seite 1216-1224
  • Language: English
  • DOI: 10.1038/s41591-018-0137-0
  • ISSN: 1078-8956; 1546-170X
  • Origination:
  • Footnote: