• Media type: E-Article
  • Title: A pathogenic proteolysis–resistant huntingtin isoform induced by an antisense oligonucleotide maintains huntingtin function
  • Contributor: Kim, Hyeongju; Lenoir, Sophie; Helfricht, Angela; Jung, Taeyang; Karneva, Zhana K.; Lee, Yejin; Beumer, Wouter; van der Horst, Geert B.; Anthonijsz, Herma; Buil, Levi C.M.; van der Ham, Frits; Platenburg, Gerard J.; Purhonen, Pasi; Hebert, Hans; Humbert, Sandrine; Saudou, Frédéric; Klein, Pontus; Song, Ji-Joon
  • imprint: American Society for Clinical Investigation, 2022
  • Published in: JCI Insight
  • Language: English
  • DOI: 10.1172/jci.insight.154108
  • ISSN: 2379-3708
  • Keywords: General Medicine
  • Origination:
  • Footnote:
  • Access State: Open Access