• Media type: E-Article
  • Title: Lentivirus-mediated gene therapy corrects ribosomal biogenesis and shows promise for Diamond Blackfan anemia
  • Contributor: Giménez, Yari; Palacios, Manuel; Sánchez-Domínguez, Rebeca; Zorbas, Christiane; Peral, Jorge; Puzik, Alexander; Ugalde, Laura; Alberquilla, Omaira; Villanueva, Mariela; Río, Paula; Gálvez, Eva; Da Costa, Lydie; Strullu, Marion; Catala, Albert; Ruiz-Llobet, Anna; Segovia, Jose Carlos; Sevilla, Julián; Strahm, Brigitte; Niemeyer, Charlotte M.; Beléndez, Cristina; Leblanc, Thierry; Lafontaine, Denis L.J.; Bueren, Juan; Navarro, Susana
  • Published: American Society for Clinical Investigation, 2024
  • Published in: JCI Insight, 9 (2024) 10
  • Language: English
  • DOI: 10.1172/jci.insight.171650
  • ISSN: 2379-3708
  • Origination:
  • Footnote:
  • Access State: Open Access