• Media type: E-Article
  • Title: A phase I/II study on intracerebroventricular tralesinidase alfa in patients with Sanfilippo syndrome type B
  • Contributor: Muschol, Nicole; Koehn, Anja; von Cossel, Katharina; Okur, Ilyas; Ezgu, Fatih; Harmatz, Paul; de Castro Lopez, Maria J.; Couce, Maria Luz; Lin, Shuan-Pei; Batzios, Spyros; Cleary, Maureen; Solano, Martha; Nestrasil, Igor; Kaufman, Brian; Shaywitz, Adam J.; Maricich, Stephen M.; Kuca, Bernice; Kovalchin, Joseph; Zanelli, Eric
  • imprint: American Society for Clinical Investigation, 2023
  • Published in: Journal of Clinical Investigation
  • Language: English
  • DOI: 10.1172/jci165076
  • ISSN: 1558-8238
  • Origination:
  • Footnote:
  • Access State: Open Access