Media type: E-Article Title: Pressure for drug development in lysosomal storage disorders – a quantitative analysis thirty years beyond the US orphan drug act Contributor: Mechler, Konstantin; Mountford, William K; Hoffmann, Georg F; Ries, Markus Published: Springer Science and Business Media LLC, 2015 Published in: Orphanet Journal of Rare Diseases, 10 (2015) 1 Language: English DOI: 10.1186/s13023-015-0262-5 ISSN: 1750-1172 Origination: Footnote: Access State: Open Access