• Media type: E-Article
  • Title: TPC2 rescues lysosomal storage in mucolipidosis type IV , Niemann–Pick type C1, and Batten disease
  • Contributor: Scotto Rosato, Anna; Krogsaeter, Einar K; Jaślan, Dawid; Abrahamian, Carla; Montefusco, Sandro; Soldati, Chiara; Spix, Barbara; Pizzo, Maria Teresa; Grieco, Giuseppina; Böck, Julia; Wyatt, Amanda; Wünkhaus, Daniela; Passon, Marcel; Stieglitz, Marc; Keller, Marco; Hermey, Guido; Markmann, Sandra; Gruber‐Schoffnegger, Doris; Cotman, Susan; Johannes, Ludger; Crusius, Dennis; Boehm, Ulrich; Wahl‐Schott, Christian; Biel, Martin; [...]
  • imprint: Springer Science and Business Media LLC, 2022
  • Published in: EMBO Molecular Medicine
  • Language: English
  • DOI: 10.15252/emmm.202115377
  • ISSN: 1757-4684; 1757-4676
  • Keywords: Molecular Medicine
  • Origination:
  • Footnote:
  • Access State: Open Access