• Media type: E-Article
  • Title: Conducting an investigator-initiated randomized double-blinded intervention trial in acute decompensation of inborn errors of metabolism: Lessons from the N-Carbamylglutamate Consortium
  • Contributor: Ah Mew, Nicholas; Cnaan, Avital; McCarter, Robert; Choi, Henry; Glass, Penny; Rice, Katie; Scavo, Louis; Gillespie, Catherine W.; Diaz, George A.; Berry, Gerard T.; Wong, Derek; Konczal, Laura; McCandless, Shawn E.; Coughlin II, Curtis R.; Weisfeld-Adams, James D.; Ficicioglu, Can; Yudkoff, Mark; Enns, Gregory M.; Lichter-Konecki, Uta; Gallagher, Renata; Tuchman, Mendel
  • Published: IOS Press, 2018
  • Published in: Translational Science of Rare Diseases, 3 (2018) 3-4, Seite 157-170
  • Language: Not determined
  • DOI: 10.3233/trd-180031
  • ISSN: 2214-6490; 2214-6512
  • Origination:
  • Footnote:
  • Access State: Open Access