• Medientyp: E-Artikel
  • Titel: Efficacy and Safety of Elexacaftor/Tezacaftor/Ivacaftor in Children 6 Through 11 Years of Age with Cystic Fibrosis Heterozygous for F508del and a Minimal Function Mutation: A Phase 3b, Randomized, Placebo-controlled Study
  • Beteiligte: Mall, Marcus A.; Brugha, Rossa; Gartner, Silvia; Legg, Julian; Moeller, Alexander; Mondejar-Lopez, Pedro; Prais, Dario; Pressler, Tacjana; Ratjen, Felix; Reix, Philippe; Robinson, Paul D.; Selvadurai, Hiran; Stehling, Florian; Ahluwalia, Neil; Arteaga-Solis, Emilio; Bruinsma, Bote G.; Jennings, Mark; Moskowitz, Samuel M.; Noel, Sabrina; Tian, Simon; Weinstock, Tanya G.; Wu, Pan; Wainwright, Claire E.; Davies, Jane C.
  • Erschienen: American Thoracic Society, 2022
  • Erschienen in: American Journal of Respiratory and Critical Care Medicine
  • Sprache: Englisch
  • DOI: 10.1164/rccm.202202-0392oc
  • ISSN: 1073-449X; 1535-4970
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  • Zugangsstatus: Freier Zugang